Today, the The Rare Disease Company Coalition sent this letter to committee chairs in both houses of the U.S. Congress, reminding them of the importance of accelerated approval of therapeutics to counter rare diseases.
I applaud the Coalition for taking this important action. I encourage everyone to contact your member of congress to backstop this critical message. Call them, email them, text them, camp out at their local office until they speak to you. Whatever it takes, please.